Gene therapy can effectively treat various diseases, but for some debilitating conditions like muscular dystrophies there is ...

Clinical development and trial testing of vesleteplirsen (SRP-5051) for Duchenne muscular dystrophy (DMD) was stopped, with ...

These updates will also be presented at the American Society of Gene and Cell Therapy and Muscular Dystrophy Association 2024 Breakthroughs ... including RGX-202 for the treatment of Duchenne, ...

Sarepta Therapeutics (Nasdaq: SRPT) has announced it will cease development of SRP-5051, an experimental drug for Duchenne ...

CHARLESTOWN, Mass., Nov. 14, 2024 (GLOBE NEWSWIRE) -- (Nasdaq: SLDB) (the “Company” or “Solid”), a life sciences company ...

The company’s focus has shifted toward upcoming data readouts for sevasemten in Becker muscular dystrophy (BMD) and Duchenne muscular dystrophy (DMD), following positive results for EDG-7500 in ...

According to the Mayo Clinic, muscular dystrophy is a group of diseases that cause loss of muscle mass and progressive ...

An FDA expansion of Sarepta Therapeutics’ Duchenne muscular dystrophy (DMD) Elevidys has sparked a new surge in sales for the ...

Oppenheimer analyst Jeff Jones maintained a Buy rating on Astria Therapeutics (ATXS – Research Report) today and set a price target of ...

Netflix flexes documentary muscle with eight projects in the running for an Oscar, but National Geo, others have strong ...

We have studied such a kindred, in which 9 males have a clinically distinct X-linked muscular dystrophy that significantly differs from the Duchenne form. Moreover, using multiple diagnostic ...

WHAT IT'S ABOUT The documentary "The Remarkable Life of Ibelin" tells the story of Mats Steen, a Norwegian man with Duchenne ...